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Leukodystrophy - 153 Studies Found
Estado | Estudiar |
Recruiting |
Nombre del estudio: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells Condición:
Intervenciones: |
Completed |
Nombre del estudio: Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation Condición:
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Recruiting |
Nombre del estudio: MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis Condición:
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Completed |
Nombre del estudio: Stem Cell Transplant for Inborn Errors of Metabolism Condición:
Intervenciones: |
Active, not recruiting |
Nombre del estudio: The Natural History of Metachromatic Leukodystrophy Condición: Metachromatic Leukodystrophy Fecha: 2008-03-11 |
Recruiting |
Nombre del estudio: Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy Condición: Metachromatic Leukodystrophy Fecha: 2013-01-28 Intervenciones: Genetic: intracerebral administration of AAVrh.10cuARSA |
Completed |
Nombre del estudio: Multicenter Study of HGT-1110 Administered Intrathecally in Children With Metachromatic Leukodystrophy (MLD) Condición: Metachromatic Leukodystrophy (MLD) Fecha: 2011-12-14 Intervenciones: Biological: Recombinant human arylsulfatase A 6 patients treated with HGT-1110 EOW by IT injection |
Completed |
Nombre del estudio: Effect of Warfarin in the Treatment of Metachromatic Leukodystrophy Condición: Metachromatic Leukodystrophy Fecha: 2008-05-21 Intervenciones: Drug: Warfarin Oral administration (QD), variable dosage: patients will undergo blood test for PT/INR at |
Withdrawn |
Nombre del estudio: An Observational Study of Pediatric Subjects With Globoid Cell Leukodystrophy (GLD) Condición: Leukodystrophy, Globoid Cell Fecha: 2010-03-24 |