Search for Clinical Trial Results

Sandhoff Disease - 14 Studies Found
Status | Study |
Completed |
Study Name: Pyrimethamine as a Treatment for Late-Onset GM2-gangliosidosis (Tay-Sachs and Sandhoff Disease) Condition:
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Completed |
Study Name: Gene Therapy for Tay-Sachs Disease Condition:
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Completed |
Study Name: Pharmacokinetics, Safety and Tolerability of Zavesca (Miglustat) in Patients With Infantile Onset Gangliosidosis: Single and Steady State Oral Doses Condition:
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Recruiting |
Study Name: Synergistic Enteral Regimen for Treatment of the Gangliosidoses Condition:
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Recruiting |
Study Name: A Natural History Study of the Gangliosidoses Condition:
Date: 2014-10-23 |
Completed |
Study Name: HSCT for High Risk Inherited Inborn Errors Condition:
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Recruiting |
Study Name: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells Condition:
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Active, not recruiting |
Study Name: Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders Condition:
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